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Old Wed Jan 18, 2012, 12:54 PM
Marlene Marlene is offline
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Join Date: Oct 2006
Location: Springfield, VA
Posts: 1,406
Thank for the insights on this enzyme. I looked a bit further and found that it's used to treat genetic disorder where the liver cannot release what it manufactures it into the bloodstream causing a deficiency in it. Thereby, causing lung and liver problems. It's used to treat lung problems in these individuals. It's a once weekly IV infusion. The enzyme is derived from pooled blood plasma.

And since it is already being used in humans, I too think it's a "no-brainer" to move forward. I guess all they need is $$$$ and some patients. What's difficult though is that the patient has had to fail all other conventional therapies. And since it's not a drug, funding may be difficult to get.
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Marlene, wife to John DX w/SAA April 2002, Stable partial remission; Treated with High Dose Cytoxan, Johns Hopkins, June 2002. Final phlebotomy 11/2016. As of July 2021 HGB 12.0, WBC 4.70/ANC 3.85, Plts 110K.
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