Thanks for posting the link. It seems many people have alreasy benefited from this.
I wonder how gene therapy can work for MDS, and if and when it can be offered as a potential treatment option.
For low risk MDS, there is very little in the pipeline of treatment options, even though majority of MDS is low risk.
Mother age 79, dx MDS RCMD low risk del 20q April 2013, no response to EPO, Danazol. pRBC tx dependent - 2 units every 3-4 weeks, exjade Dec 2013 - Mar2014, restarted Dec 2014